• Effects of gene therapy on cardiovascular symptoms of lysosomal storage diseases 

      Poletto, Édina; Pasqualim, Gabriela; Giugliani, Roberto; Matte, Ursula da Silveira; Baldo, Guilherme (2019) [Artigo de periódico]
      Lysosomal storage diseases (LSDs) are inherited conditions caused by impaired lysosomal function and consequent substrate storage, leading to a range of clinical manifestations, including cardiovascular disease. This may ...