Navegação por Assunto "Signs and symptom"
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Clinical profile among brazilian Mucopolysaccharidosis type II patients : subgroup analysis from the Hunter Outcome Survey
(2023) [Artigo de periódico]Mucopolysaccharidosis type II (MPS II) is a rare genetic, multiorgan disease. Little information about the Brazilian context is available to date; thus, this descriptive subgroup analysis was conducted on Brazilian data ...