Navegação por Autor "Rust, Stewart"

Resultados 1-1 de 1

    • Therapy development for the mucopolysaccharidoses : updated consensus recommendations for neuropsychological endpoints 

      Van der Lee, Johanna Hanneke; Morton, Jonathan; Adams, Heather R.; Clarke, Lorne A.; Eisengart, Julie B.; Escolar, Maria Luisa; Giugliani, Roberto; Harmatz, Paul; Hogan, Melissa; Kearney, Shauna; Muenzer, Joseph; Muschol, Nicole; Rust, Stewart; Saville, Benjamin R.; Semrud-Clikeman, Margaret T.; Wang, Raymond Y.; Shapiro, Elsa G. (2020) [Artigo de periódico]
      Neurological dysfunction represents a significant clinical component of many of the mucopolysaccharidoses (also known as MPS disorders). The accurate and consistent assessment of neuropsychological function is essential ...